The latest in features and updates that are relevant to sickle cell research, from publications around the world.

CRISPR/Cas9 Gene-Editing Therapy, CTX001™ at European Hematology Association Annual Meeting

08 Jul 2021

CTX001 is being investigated in two ongoing Phase 1/2 clinical trials as a potential one-time therapy for patients suffering from transfusion-dependent beta thalassemia (TDT) and severe sickle cell disease (SCD). In total, more than 40 patients have been dosed across both studies to date. All 15 patients with TDT, including six who have the beta […]

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Treatment of Acute Pain in Adults With Sickle Cell Disease in an Infusion Center Versus the Emergency Department

06 Jul 2021

Patients with sickle cell disease (SCD) have vaso-occlusive crises (VOCs). Infusion centers (ICs) are alternatives to emergency department (ED) care and may improve patient outcomes.

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Advocate for sickle cell disease awareness shares blood shortage concerns

23 Jun 2021

The American Red Cross says we are in the midst of a severe blood donation shortage. “People with sickle cell disease depend on blood transfusions regularly.”

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