Jewel is a teenager living with sickle cell disease. She and her mother, Paula make informed decision about participating in clinical studies.
Ada Gonzalez lives with sickle cell disease and enrolled in a clinical study decades ago that she benefits from today.
Andre, an adult living with sickle cell disease, talks about the need for treatment options for the aging and future generations with sickle cell disease.
To identify treatments that do not rely only on opioids or other medications. Participants will use their smartphone to answer questionnaires and interact with a mobile application
18 to 28
Hb Sβ0 thalassemia
Hb Sβ+ thalassemia
To study blood clotting in SCD because it is the most common cause of vascular death after a heart attack or stroke. To study blood clotting in SCD because it is the most common ca
08 Jul 2021
CTX001 is being investigated in two ongoing Phase 1/2 clinical trials as a potential one-time therapy for patients suffering from transfusion-dependent beta thalassemia (TDT) and severe sickle cell disease (SCD). In total, more than 40 patients have been dosed across both studies to date. All 15 patients with TDT, including six who have the beta […]Learn more
06 Jul 2021
Patients with sickle cell disease (SCD) have vaso-occlusive crises (VOCs). Infusion centers (ICs) are alternatives to emergency department (ED) care and may improve patient outcomes.Learn more
23 Jun 2021
The American Red Cross says we are in the midst of a severe blood donation shortage. “People with sickle cell disease depend on blood transfusions regularly.”Learn more
We send occasional updates that feature new trials, and other great tips. We will not spam you.